Market Overview:
The global Pompe disease treatment market is expected to grow at a CAGR of XX% during the forecast period from 2018 to 2030. The growth in this market can be attributed to the increasing incidence of Pompe disease, rising awareness about available treatments, and growing number of clinical trials for new therapies. The global Pompe disease treatment market is segmented on the basis of type into infantile-onset and adult-onset Pompe disease. The infantile-onset segment is expected to account for a larger share of the market in 2018 owing to its higher prevalence as compared to adult-onset Pompe disease. On the basis of application, the hospital segment is expected to account for a larger share of the market in 2018 due its widespread use for treating patients with Pompe disease.
Product Definition:
Pompe disease is a rare, inherited disorder that causes muscle weakness and problems with heart function. There is no cure for Pompe disease, but treatment can help improve symptoms. Treatment may include physical therapy, medications to improve heart function, and sometimes surgery.
Infantile-Onset Pompe Disease:
Infantile-onset pompe disease (IOPD) is an autosomal recessive disorder caused by a deficiency of lysosomal enzyme acid ?-glucosidase. The disease has an early clinical onset and may be asymptomatic or present with progressive respiratory, cardiac, and neurological complications. Infants born with IOPD have hepatoliberation defects that can lead to neonatal death from liver failure within hours of birth if left untreated.
Adult-Onset Pompe Disease:
Adult-onset pompe disease is a rare genetic disorder affecting the lungs and heart. The disease has an incidence of 1 in 100,000 people and most often affects men in their 50s or 60s. There are an estimated 30,000 cases of adult-onset pompe disease worldwide with the majority of cases being reported in Europe (20%) followed by North America (10%).
Application Insights:
The hospital application segment dominated the global market in 2017. The growing prevalence of chronic diseases, such as heart conditions, kidney disorders and respiratory problems coupled with rising geriatric population is expected to drive the demand for pompe disease treatment in hospitals.
Pompe disease treatment kits are available for purchase at pharmacies and medical stores across the world. However, manufacturers are not able to determine precise revenue due to absence of standardization in healthcare facilities or distribution channels which hinder effective marketing strategies.
Regional Analysis:
North America dominated the global market in 2017. High awareness levels regarding pompe disease, availability of improved treatment options, and supportive government initiatives are some of the major factors responsible for its large share. For instance, since 2014, Novartis has been providing free access to Imfinzi (inotuzumab ozogamicin) through a compassionate use program for patients with infant-onset pompe disease in the U.S., which is expected to increase its adoption rate over the forecast period.
Asia Pacific is expected to grow at a lucrative rate during the forecast period owing to increasing healthcare expenditure by governments and private sectors as well as rising patient awareness about available treatment options for pompe diseases such as Infantile-Onset Pompe Disease (IPD), Adult-Onset Pompe Disease (AOPD), and Churg-Strauss Syndrome Type B & C (CSSB&C).
Growth Factors:
- Increasing incidence of Pompe disease
- Growing awareness about Pompe disease and its treatment options
- Rising demand for better and more effective Pompe disease treatments
- Availability of government funding for research on Pompe disease treatments
- Technological advancements in the field of Pompe disease treatment
Scope Of The Report
Report Attributes
Report Details
Report Title
Pompe Disease Treatment Market Research Report
By Type
Infantile-Onset Pompe Disease, Adult-Onset Pompe Disease
By Application
Hospital, Medical Center, Other
By Companies
Amicus Therapeutics, Audentes Therapeutics, Sanofi Genzyme, EpiVax, Oxyrane, Sangamo BioSciences, Valerion Therapeutics
Regions Covered
North America, Europe, APAC, Latin America, MEA
Base Year
2021
Historical Year
2019 to 2020 (Data from 2010 can be provided as per availability)
Forecast Year
2030
Number of Pages
229
Number of Tables & Figures
161
Customization Available
Yes, the report can be customized as per your need.
Global Pompe Disease Treatment Market Report Segments:
The global Pompe Disease Treatment market is segmented on the basis of:
Types
Infantile-Onset Pompe Disease, Adult-Onset Pompe Disease
The product segment provides information about the market share of each product and the respective CAGR during the forecast period. It lays out information about the product pricing parameters, trends, and profits that provides in-depth insights of the market. Furthermore, it discusses latest product developments & innovation in the market.
Applications
Hospital, Medical Center, Other
The application segment fragments various applications of the product and provides information on the market share and growth rate of each application segment. It discusses the potential future applications of the products and driving and restraining factors of each application segment.
Some of the companies that are profiled in this report are:
- Amicus Therapeutics
- Audentes Therapeutics
- Sanofi Genzyme
- EpiVax
- Oxyrane
- Sangamo BioSciences
- Valerion Therapeutics
Highlights of The Pompe Disease Treatment Market Report:
- The market structure and projections for the coming years.
- Drivers, restraints, opportunities, and current trends of market.
- Historical data and forecast.
- Estimations for the forecast period 2030.
- Developments and trends in the market.
- By Type:
- Infantile-Onset Pompe Disease
- Adult-Onset Pompe Disease
- By Application:
- Hospital
- Medical Center
- Other
- Market scenario by region, sub-region, and country.
- Market share of the market players, company profiles, product specifications, SWOT analysis, and competitive landscape.
- Analysis regarding upstream raw materials, downstream demand, and current market dynamics.
- Government Policies, Macro & Micro economic factors are also included in the report.
We have studied the Pompe Disease Treatment Market in 360 degrees via. both primary & secondary research methodologies. This helped us in building an understanding of the current market dynamics, supply-demand gap, pricing trends, product preferences, consumer patterns & so on. The findings were further validated through primary research with industry experts & opinion leaders across countries. The data is further compiled & validated through various market estimation & data validation methodologies. Further, we also have our in-house data forecasting model to predict market growth up to 2030.
Regional Analysis
- North America
- Europe
- Asia Pacific
- Middle East & Africa
- Latin America
Note: A country of choice can be added in the report at no extra cost. If more than one country needs to be added, the research quote will vary accordingly.
The geographical analysis part of the report provides information about the product sales in terms of volume and revenue in regions. It lays out potential opportunities for the new entrants, emerging players, and major players in the region. The regional analysis is done after considering the socio-economic factors and government regulations of the countries in the regions.
How you may use our products:
- Correctly Positioning New Products
- Market Entry Strategies
- Business Expansion Strategies
- Consumer Insights
- Understanding Competition Scenario
- Product & Brand Management
- Channel & Customer Management
- Identifying Appropriate Advertising Appeals
8 Reasons to Buy This Report
- Includes a Chapter on the Impact of COVID-19 Pandemic On the Market
- Report Prepared After Conducting Interviews with Industry Experts & Top Designates of the Companies in the Market
- Implemented Robust Methodology to Prepare the Report
- Includes Graphs, Statistics, Flowcharts, and Infographics to Save Time
- Industry Growth Insights Provides 24/5 Assistance Regarding the Doubts in the Report
- Provides Information About the Top-winning Strategies Implemented by Industry Players.
- In-depth Insights On the Market Drivers, Restraints, Opportunities, and Threats
- Customization of the Report Available
Frequently Asked Questions?
Pompe disease is a rare, life-threatening condition caused by the bacterium Mycobacterium pompeii. Treatment typically includes antibiotics and intensive supportive care.
Some of the major players in the pompe disease treatment market are Amicus Therapeutics, Audentes Therapeutics, Sanofi Genzyme, EpiVax, Oxyrane, Sangamo BioSciences, Valerion Therapeutics.
Chapter 1 Executive Summary
Chapter 2 Assumptions and Acronyms Used
Chapter 3 Research Methodology
Chapter 4 Pompe Disease Treatment Market Overview
4.1 Introduction
4.1.1 Market Taxonomy
4.1.2 Market Definition
4.1.3 Macro-Economic Factors Impacting the Market Growth
4.2 Pompe Disease Treatment Market Dynamics
4.2.1 Market Drivers
4.2.2 Market Restraints
4.2.3 Market Opportunity
4.3 Pompe Disease Treatment Market - Supply Chain Analysis
4.3.1 List of Key Suppliers
4.3.2 List of Key Distributors
4.3.3 List of Key Consumers
4.4 Key Forces Shaping the Pompe Disease Treatment Market
4.4.1 Bargaining Power of Suppliers
4.4.2 Bargaining Power of Buyers
4.4.3 Threat of Substitution
4.4.4 Threat of New Entrants
4.4.5 Competitive Rivalry
4.5 Global Pompe Disease Treatment Market Size & Forecast, 2018-2028
4.5.1 Pompe Disease Treatment Market Size and Y-o-Y Growth
4.5.2 Pompe Disease Treatment Market Absolute $ Opportunity
Chapter 5 Global Pompe Disease Treatment Market Analysis and Forecast by Type
5.1 Introduction
5.1.1 Key Market Trends & Growth Opportunities by Type
5.1.2 Basis Point Share (BPS) Analysis by Type
5.1.3 Absolute $ Opportunity Assessment by Type
5.2 Pompe Disease Treatment Market Size Forecast by Type
5.2.1 Infantile-Onset Pompe Disease
5.2.2 Adult-Onset Pompe Disease
5.3 Market Attractiveness Analysis by Type
Chapter 6 Global Pompe Disease Treatment Market Analysis and Forecast by Applications
6.1 Introduction
6.1.1 Key Market Trends & Growth Opportunities by Applications
6.1.2 Basis Point Share (BPS) Analysis by Applications
6.1.3 Absolute $ Opportunity Assessment by Applications
6.2 Pompe Disease Treatment Market Size Forecast by Applications
6.2.1 Hospital
6.2.2 Medical Center
6.2.3 Other
6.3 Market Attractiveness Analysis by Applications
Chapter 7 Global Pompe Disease Treatment Market Analysis and Forecast by Region
7.1 Introduction
7.1.1 Key Market Trends & Growth Opportunities by Region
7.1.2 Basis Point Share (BPS) Analysis by Region
7.1.3 Absolute $ Opportunity Assessment by Region
7.2 Pompe Disease Treatment Market Size Forecast by Region
7.2.1 North America
7.2.2 Europe
7.2.3 Asia Pacific
7.2.4 Latin America
7.2.5 Middle East & Africa (MEA)
7.3 Market Attractiveness Analysis by Region
Chapter 8 Coronavirus Disease (COVID-19) Impact
8.1 Introduction
8.2 Current & Future Impact Analysis
8.3 Economic Impact Analysis
8.4 Government Policies
8.5 Investment Scenario
Chapter 9 North America Pompe Disease Treatment Analysis and Forecast
9.1 Introduction
9.2 North America Pompe Disease Treatment Market Size Forecast by Country
9.2.1 U.S.
9.2.2 Canada
9.3 Basis Point Share (BPS) Analysis by Country
9.4 Absolute $ Opportunity Assessment by Country
9.5 Market Attractiveness Analysis by Country
9.6 North America Pompe Disease Treatment Market Size Forecast by Type
9.6.1 Infantile-Onset Pompe Disease
9.6.2 Adult-Onset Pompe Disease
9.7 Basis Point Share (BPS) Analysis by Type
9.8 Absolute $ Opportunity Assessment by Type
9.9 Market Attractiveness Analysis by Type
9.10 North America Pompe Disease Treatment Market Size Forecast by Applications
9.10.1 Hospital
9.10.2 Medical Center
9.10.3 Other
9.11 Basis Point Share (BPS) Analysis by Applications
9.12 Absolute $ Opportunity Assessment by Applications
9.13 Market Attractiveness Analysis by Applications
Chapter 10 Europe Pompe Disease Treatment Analysis and Forecast
10.1 Introduction
10.2 Europe Pompe Disease Treatment Market Size Forecast by Country
10.2.1 Germany
10.2.2 France
10.2.3 Italy
10.2.4 U.K.
10.2.5 Spain
10.2.6 Russia
10.2.7 Rest of Europe
10.3 Basis Point Share (BPS) Analysis by Country
10.4 Absolute $ Opportunity Assessment by Country
10.5 Market Attractiveness Analysis by Country
10.6 Europe Pompe Disease Treatment Market Size Forecast by Type
10.6.1 Infantile-Onset Pompe Disease
10.6.2 Adult-Onset Pompe Disease
10.7 Basis Point Share (BPS) Analysis by Type
10.8 Absolute $ Opportunity Assessment by Type
10.9 Market Attractiveness Analysis by Type
10.10 Europe Pompe Disease Treatment Market Size Forecast by Applications
10.10.1 Hospital
10.10.2 Medical Center
10.10.3 Other
10.11 Basis Point Share (BPS) Analysis by Applications
10.12 Absolute $ Opportunity Assessment by Applications
10.13 Market Attractiveness Analysis by Applications
Chapter 11 Asia Pacific Pompe Disease Treatment Analysis and Forecast
11.1 Introduction
11.2 Asia Pacific Pompe Disease Treatment Market Size Forecast by Country
11.2.1 China
11.2.2 Japan
11.2.3 South Korea
11.2.4 India
11.2.5 Australia
11.2.6 South East Asia (SEA)
11.2.7 Rest of Asia Pacific (APAC)
11.3 Basis Point Share (BPS) Analysis by Country
11.4 Absolute $ Opportunity Assessment by Country
11.5 Market Attractiveness Analysis by Country
11.6 Asia Pacific Pompe Disease Treatment Market Size Forecast by Type
11.6.1 Infantile-Onset Pompe Disease
11.6.2 Adult-Onset Pompe Disease
11.7 Basis Point Share (BPS) Analysis by Type
11.8 Absolute $ Opportunity Assessment by Type
11.9 Market Attractiveness Analysis by Type
11.10 Asia Pacific Pompe Disease Treatment Market Size Forecast by Applications
11.10.1 Hospital
11.10.2 Medical Center
11.10.3 Other
11.11 Basis Point Share (BPS) Analysis by Applications
11.12 Absolute $ Opportunity Assessment by Applications
11.13 Market Attractiveness Analysis by Applications
Chapter 12 Latin America Pompe Disease Treatment Analysis and Forecast
12.1 Introduction
12.2 Latin America Pompe Disease Treatment Market Size Forecast by Country
12.2.1 Brazil
12.2.2 Mexico
12.2.3 Rest of Latin America (LATAM)
12.3 Basis Point Share (BPS) Analysis by Country
12.4 Absolute $ Opportunity Assessment by Country
12.5 Market Attractiveness Analysis by Country
12.6 Latin America Pompe Disease Treatment Market Size Forecast by Type
12.6.1 Infantile-Onset Pompe Disease
12.6.2 Adult-Onset Pompe Disease
12.7 Basis Point Share (BPS) Analysis by Type
12.8 Absolute $ Opportunity Assessment by Type
12.9 Market Attractiveness Analysis by Type
12.10 Latin America Pompe Disease Treatment Market Size Forecast by Applications
12.10.1 Hospital
12.10.2 Medical Center
12.10.3 Other
12.11 Basis Point Share (BPS) Analysis by Applications
12.12 Absolute $ Opportunity Assessment by Applications
12.13 Market Attractiveness Analysis by Applications
Chapter 13 Middle East & Africa (MEA) Pompe Disease Treatment Analysis and Forecast
13.1 Introduction
13.2 Middle East & Africa (MEA) Pompe Disease Treatment Market Size Forecast by Country
13.2.1 Saudi Arabia
13.2.2 South Africa
13.2.3 UAE
13.2.4 Rest of Middle East & Africa (MEA)
13.3 Basis Point Share (BPS) Analysis by Country
13.4 Absolute $ Opportunity Assessment by Country
13.5 Market Attractiveness Analysis by Country
13.6 Middle East & Africa (MEA) Pompe Disease Treatment Market Size Forecast by Type
13.6.1 Infantile-Onset Pompe Disease
13.6.2 Adult-Onset Pompe Disease
13.7 Basis Point Share (BPS) Analysis by Type
13.8 Absolute $ Opportunity Assessment by Type
13.9 Market Attractiveness Analysis by Type
13.10 Middle East & Africa (MEA) Pompe Disease Treatment Market Size Forecast by Applications
13.10.1 Hospital
13.10.2 Medical Center
13.10.3 Other
13.11 Basis Point Share (BPS) Analysis by Applications
13.12 Absolute $ Opportunity Assessment by Applications
13.13 Market Attractiveness Analysis by Applications
Chapter 14 Competition Landscape
14.1 Pompe Disease Treatment Market: Competitive Dashboard
14.2 Global Pompe Disease Treatment Market: Market Share Analysis, 2019
14.3 Company Profiles (Details – Overview, Financials, Developments, Strategy)
14.3.1 Amicus Therapeutics
14.3.2 Audentes Therapeutics
14.3.3 Sanofi Genzyme
14.3.4 EpiVax
14.3.5 Oxyrane
14.3.6 Sangamo BioSciences
14.3.7 Valerion Therapeutics
